Gene Therapy

[lauerz]

A few years ago, a clinical trial began in France in the hope of curing children with a type of genetic immune deficiency called SCID-X1. Children with this disease have a defective gene, called gamma-c, which prevents a subset of the cells of the immune system from forming, and predisposes the children to life-threatening infections. In an attempt to cure the children—who would otherwise die at a young age—physicians used gene therapy to provide them with normal gamma-c genes.

http://www.sumanasinc.com/scienceinfocus/sif_genetherapy.html

Gene therapy success 'reverses' blindness
http://www.youtube.com/watch?v=d_YJZn-ft_Q